| Molecular remission of infant B-ALL after infusion of universal TALEN gene-edited CAR T cells W Qasim, H Zhan, S Samarasinghe, S Adams, P Amrolia, S Stafford, ... Science translational medicine 9 (374), eaaj2013, 2017 | 951 | 2017 |
| Comprehensive rare variant analysis via whole-genome sequencing to determine the molecular pathology of inherited retinal disease KJ Carss, G Arno, M Erwood, J Stephens, A Sanchis-Juan, S Hull, K Megy, ... The American Journal of Human Genetics 100 (1), 75-90, 2017 | 409 | 2017 |
| Long-term outcome and lineage-specific chimerism in 194 patients with Wiskott-Aldrich syndrome treated by hematopoietic cell transplantation in the period 1980-2009: an … D Moratto, S Giliani, C Bonfim, E Mazzolari, A Fischer, HD Ochs, AJ Cant, ... Blood, The Journal of the American Society of Hematology 118 (6), 1675-1684, 2011 | 330 | 2011 |
| Human coronavirus OC43 associated with fatal encephalitis S Morfopoulou, JR Brown, EG Davies, G Anderson, A Virasami, W Qasim, ... New England Journal of Medicine 375 (5), 497-498, 2016 | 320 | 2016 |
| Genome-edited, donor-derived allogeneic anti-CD19 chimeric antigen receptor T cells in paediatric and adult B-cell acute lymphoblastic leukaemia: results of two phase 1 studies R Benjamin, C Graham, D Yallop, A Jozwik, OC Mirci-Danicar, G Lucchini, ... The Lancet 396 (10266), 1885-1894, 2020 | 260 | 2020 |
| Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: an international multicenter retrospective study F Barzaghi, LCA Hernandez, B Neven, S Ricci, ZY Kucuk, JJ Bleesing, ... Journal of Allergy and Clinical Immunology 141 (3), 1036-1049. e5, 2018 | 255 | 2018 |
| Elimination of human leukemia cells in NOD/SCID mice by WT1-TCR gene–transduced human T cells SA Xue, L Gao, D Hart, R Gillmore, W Qasim, A Thrasher, J Apperley, ... Blood 106 (9), 3062-3067, 2005 | 244 | 2005 |
| Automated manufacturing of chimeric antigen receptor T cells for adoptive immunotherapy using CliniMACS prodigy U Mock, L Nickolay, B Philip, GWK Cheung, H Zhan, ICD Johnston, ... Cytotherapy 18 (8), 1002-1011, 2016 | 221 | 2016 |
| Immunotherapy of HCC metastases with autologous T cell receptor redirected T cells, targeting HBsAg in a liver transplant patient W Qasim, M Brunetto, AJ Gehring, SA Xue, A Schurich, A Khakpoor, ... Journal of hepatology 62 (2), 486-491, 2015 | 215 | 2015 |
| Loss-of-function nuclear factor κB subunit 1 (NFKB1) variants are the most common monogenic cause of common variable immunodeficiency in Europeans P Tuijnenburg, HL Allen, SO Burns, D Greene, MH Jansen, E Staples, ... Journal of allergy and clinical immunology 142 (4), 1285-1296, 2018 | 209 | 2018 |
| Astrovirus VA1/HMO-C: an increasingly recognized neurotropic pathogen in immunocompromised patients JR Brown, S Morfopoulou, J Hubb, WA Emmett, W Ip, D Shah, T Brooks, ... Clinical Infectious Diseases 60 (6), 881-888, 2015 | 200 | 2015 |
| Clinical and immunological manifestations of patients with atypical severe combined immunodeficiency K Felgentreff, R Perez-Becker, C Speckmann, K Schwarz, K Kalwak, ... Clinical immunology 141 (1), 73-82, 2011 | 195 | 2011 |
| Treosulfan-based conditioning regimens for hematopoietic stem cell transplantation in children with primary immunodeficiency: United Kingdom experience MA Slatter, K Rao, P Amrolia, T Flood, M Abinun, S Hambleton, Z Nademi, ... Blood, The Journal of the American Society of Hematology 117 (16), 4367-4375, 2011 | 163 | 2011 |
| Impact of viral reactivations in the era of pre-emptive antiviral drug therapy following allogeneic haematopoietic SCT in paediatric recipients P Hiwarkar, HB Gaspar, K Gilmour, M Jagani, R Chiesa, N Bennett-Rees, ... Bone marrow transplantation 48 (6), 803-808, 2013 | 161 | 2013 |
| T-cell receptor αβ+ and CD19+ cell–depleted haploidentical and mismatched hematopoietic stem cell transplantation in primary immune deficiency RM Shah, R Elfeky, Z Nademi, W Qasim, P Amrolia, R Chiesa, K Rao, ... Journal of Allergy and Clinical Immunology 141 (4), 1417-1426. e1, 2018 | 140 | 2018 |
| Omission of in vivo T‐cell depletion promotes rapid expansion of naïve CD4+ cord blood lymphocytes and restores adaptive immunity within 2 months after … R Chiesa, K Gilmour, W Qasim, S Adams, AJJ Worth, H Zhan, ... British journal of haematology 156 (5), 656-666, 2012 | 139 | 2012 |
| Inherited GINS1 deficiency underlies growth retardation along with neutropenia and NK cell deficiency J Cottineau, MC Kottemann, FP Lach, YH Kang, F Vély, EK Deenick, ... The Journal of clinical investigation 127 (5), 1991-2006, 2017 | 127 | 2017 |
| Allogeneic hematopoietic stem-cell transplantation for leukocyte adhesion deficiency W Qasim, M Cavazzana-Calvo, EG Davies, J Davis, M Duval, G Eames, ... Pediatrics 123 (3), 836-840, 2009 | 126 | 2009 |
| Long terminal repeat CRISPR-CAR-coupled “universal” T cells mediate potent anti-leukemic effects C Georgiadis, R Preece, L Nickolay, A Etuk, A Petrova, D Ladon, A Danyi, ... Molecular Therapy 26 (5), 1215-1227, 2018 | 125 | 2018 |
| Phenotypic Characterization of EIF2AK4 Mutation Carriers in a Large Cohort of Patients Diagnosed Clinically With Pulmonary Arterial Hypertension C Hadinnapola, M Bleda, M Haimel, N Screaton, A Swift, P Dorfmüller, ... Circulation 136 (21), 2022-2033, 2017 | 125 | 2017 |
